The Use of Biomarkers to Advance Clinical Trials in Rare Genetic Disorders
Time: 1:50 pm
day: Day 1 Track A PM
Details:
- How biomarkers are used for clinical trials of rare genetic disorders as compared to oncology
- Example of biomarker usage to understand the PD/safety of gene editing based therapy, EDIT-301, in the treatment of sickle cell disease.
